Health Matters

GENE THERAPY IS BECOMING a powerful way to treat challenging diseases that don’t respond to traditional treatments, and researchers now report the first success in modifying genes to slow Huntington’s disease.

- - By Alice Park

"I went into the trial cautiously optimistic but very anxious, as one does when starting a gene-therapy trial," says Dr. Sarah Tabrizi, director of the University College London Huntington’s Disease Center. “I was blown away when I saw all of the data and it was very, very clear that the gene therapy worked.”