Essayer OR - Gratuit

'This feels one step closer to living without a reminder we even have cystic fibrosis. There's a wonderful future on the horizon'

Scottish Daily Express

|

March 17, 2025

A WONDER drug that makes most signs of cystic fibrosis "vanish" has been approved in a major boost for thousands of UK sufferers.

-  Chris Riches

'This feels one step closer to living without a reminder we even have cystic fibrosis. There's a wonderful future on the horizon'

Alyftrek is so advanced that trials show patients no longer exhibit CF symptoms in vital tests.

The "next generation" drug has been backed by regulators and could be available on the NHS by late August if a medicines watchdog gives doctors the green light to use it.

Catherine Farrer, 41, mother of CF sufferer Kate, 10, said she was thrilled by the Alyftrek approval and is desperate for her daughter to have it.

She added: "We are keen to try to switch her to Alyftrek when we can." CF is a life-limiting genetic condition that affects 11,000 people in the UK, but before 2019 the NHS had no effective treatment.

However, last summer after a five-year Daily Express campaign US drug giant Vertex agreed a health service deal so that 90% of CF patients suitable for its treatments Orkambi, Symkevi and Kaftrio could access them.

Bosses at watchdog the National Institute for Health and Care Excellence are now studying the costeffectiveness of Vertex pill Alyftrek.

CF patient Carlie Pleasant was also delighted that the Medicines and Healthcare products Regulatory Agency had backed the new drug.

She said: “This feels like one step closer to living lives without being reminded we even have CF - there’s a wonderful future on the horizon.”

The mum of one, 35, added: “When I first started campaigning with the Daily Express for access to Vertex’s CF drugs back in 2019, I was spending weeks away from my baby boy Jude in hospital with lung bugs.

“In 2020 after we secured the initial deals I went on Symkevi and then the first real wonder CF drug Kaftrio - which I'm on right now. They have transformed my health and life.

PLUS D'HISTOIRES DE Scottish Daily Express

Scottish Daily Express

Loss as Brad as it gets

BRAD LYONS admits Kilmarnock’s first-half defensive debacle at Falkirk was a career low.

time to read

1 mins

November 03, 2025

Scottish Daily Express

TAV SEES RED OVER LET-OFF

that's no excuse. We have to as a team be more clinical in that game.

time to read

2 mins

November 03, 2025

Scottish Daily Express

Scottish Daily Express

'Tax change will put jobs and critical supply chains at risk'

RACHEL Reeves must reverse her planned inheritance tax changes or risk the collapse of family-run firms that are vital to growth, building chiefs have warned.

time to read

2 mins

November 03, 2025

Scottish Daily Express

Forest's owner: I will fund medical bills for fans

NOTTINGHAM Forest owner Evangelos Marinakis has vowed to fund medical treatment for any fan involved in the train knife attack.

time to read

1 min

November 03, 2025

Scottish Daily Express

150-year-old ale is a mix of old and brew

A SCOTTISH brewer is set to open one of the rarest beers in the world — a 150-year-old bottle once brewed for an Arctic expedition — to create a modern version of the historic ale.

time to read

2 mins

November 03, 2025

Scottish Daily Express

Scottish Daily Express

Biggest banks taking 'loyalty for granted'

BRITAIN’S biggest banks are taking loyalty for granted by offering customers the lowest returns on savings, says a Which? survey.

time to read

1 mins

November 03, 2025

Scottish Daily Express

Big Festive Greetings...as BFG stars in Christmas ad

ROALD Dahl's much-loved BFG is the star of Sainsbury's new “feelgood” Christmas TV ad.

time to read

1 min

November 03, 2025

Scottish Daily Express

Parker's rage at judges

ZACH PARKER accused the judges of stealing his children's futures after Joshua Buatsi won their clash on points.

time to read

1 min

November 03, 2025

Scottish Daily Express

Rabbit chews painfully slow

OUR VET DAVID GRANT WORKS HIS MAGIC

time to read

2 mins

November 03, 2025

Scottish Daily Express

Scottish Daily Express

MAROON THE HOUSES!

Magnusson is flitting in perfectly in Edinburgh but he won't be drawn on end-of-season title deeds

time to read

3 mins

November 03, 2025

Listen

Translate

Share

-
+

Change font size