TODDLER Teddi Shaw is the first UK child to receive a gene therapy treatment costing millions on the NHS for a rare deadly genetic condition.
The 20-month-old inherited the life-limiting condition metachromatic leukodystrophy (MLD). It affects one in 40,000 babies and causes loss of nervous system and brain function, leading to a life expectancy of between five and eight years.
Revolutionary treatment Libmeldy, with a list price of £2.8 million, is a one-off gene therapy and was the most expensive drug in the world when NHS England started negotiating a significant discount.
It works by removing the child's stem cells and replacing the faulty gene that causes MLD before re-injecting the treated cells.
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